Disease ID | Source | Name | Description |
614923 | OMIM | Branched-chain ketoacid dehydrogenase kinase deficiency (BCKDKD) | A metabolic disorder characterized by autism, epilepsy, intellectual disability, and reduced branched-chain amino acids. The disease is caused by variants affecting the gene represented in this entry. A diet enriched in branched amino acids (BCAAs) allows to normalize plasma BCAA levels. This suggests that it may be possible to treat patients with mutations in BCKDK with BCAA supplementation. |